{"id":16773,"date":"2019-06-11T00:00:00","date_gmt":"2019-06-11T04:00:00","guid":{"rendered":"https:\/\/genomequebec.com\/actualites-et-publications\/phase-2-study-of-cystinosis-treatment-receives-authorization-of-clinical-trial-application-by-health-canada\/"},"modified":"2019-06-11T00:00:00","modified_gmt":"2019-06-11T04:00:00","slug":"phase-2-study-of-cystinosis-treatment-receives-authorization-of-clinical-trial-application-by-health-canada","status":"publish","type":"post","link":"https:\/\/genomequebec.com\/en\/news-and-publications\/phase-2-study-of-cystinosis-treatment-receives-authorization-of-clinical-trial-application-by-health-canada\/","title":{"rendered":"Phase 2 study of cystinosis treatment receives authorization of clinical trial application by Health Canada"},"content":{"rendered":"<p>Funded by G\u00e9nome Qu\u00e9bec and Genome Canada\u00a0<span>under the Genome Canada\u00a0<\/span><em>Genomic Applications Partnership Program <\/em>(GAPP), this trial will be led by\u00a0Dr.\u00a0Paul Goodyer, a professor of pediatrics at\u00a0McGill University\u00a0and recognized leader in hereditary renal disease.\u00a0<\/p>\n<p>ELX-02 has the\u00a0<span>potential to improve the lives of cystinosis* patients. In fact, researchs led to this day by Dr. Goodyer&#8217;s team showed that this molecule\u00a0<span>decreases the cystine content in cellular and animal models.<\/span><\/span><\/p>\n<p><span><span>Dr. Goodyer works in partnership with Eloxx Pharmaceuticals, an american\u00a0<span>biopharmaceutical company dedicated to the discovery and development of therapeutics to treat cystic fibrosis, cystinosis, inherited retinal disorders, and other diseases caused by nonsense mutations.\u00a0<\/span><\/span><\/span><\/p>\n<p><span><br \/><\/span><\/p>\n<p><span><a href=\"https:\/\/investors.eloxxpharma.com\/news-releases\/news-release-details\/eloxx-pharmaceuticals-phase-2-study-elx-02-cystinosis-receives\" target=\"_blank\" rel=\"noopener\">Read Eloxx&#8217;s press release\u00a0<\/a><\/span><\/p>\n<p><a href=\"https:\/\/www.genomequebec.com\/214-en\/project\/novel-aminoglycoside-readthrough-therapy-for-nonsense-mutations\/\" target=\"_blank\" rel=\"noopener\">Learn more about Dr. Paul Goodyer&#8217;s project<\/a><\/p>\n<p>\u00a0<\/p>\n<p><span>* <em>Cystinosis is a metabolic disease characterized by an accumulation of cystine inside the lysosomes, causing damage in different organs and tissues, particularly in the kidneys and eyes.<\/em> <a href=\"https:\/\/www.orpha.net\/consor\/cgi-bin\/OC_Exp.php?lng=EN&#038;Expert=213\" target=\"_blank\" rel=\"noopener\">Source\u00a0<\/a><\/span><\/p>\n","protected":false},"excerpt":{"rendered":"<p>Funded by G\u00e9nome Qu\u00e9bec and Genome Canada\u00a0under the Genome Canada\u00a0Genomic Applications Partnership Program (GAPP), this trial will be led by\u00a0Dr.\u00a0Paul Goodyer, a professor of pediatrics at\u00a0McGill University\u00a0and recognized leader in&hellip;<\/p>\n","protected":false},"author":1,"featured_media":16210,"comment_status":"open","ping_status":"open","sticky":false,"template":"","format":"standard","meta":{"_acf_changed":false,"_relevanssi_hide_post":"","_relevanssi_hide_content":"","_relevanssi_pin_for_all":"","_relevanssi_pin_keywords":"","_relevanssi_unpin_keywords":"","_relevanssi_related_keywords":"","_relevanssi_related_include_ids":"","_relevanssi_related_exclude_ids":"","_relevanssi_related_no_append":"","_relevanssi_related_not_related":"","_relevanssi_related_posts":"","_relevanssi_noindex_reason":"","footnotes":""},"categories":[294],"tags":[],"class_list":["post-16773","post","type-post","status-publish","format-standard","has-post-thumbnail","hentry","category-nouvelles"],"acf":[],"_links":{"self":[{"href":"https:\/\/genomequebec.com\/en\/wp-json\/wp\/v2\/posts\/16773","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/genomequebec.com\/en\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/genomequebec.com\/en\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/genomequebec.com\/en\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/genomequebec.com\/en\/wp-json\/wp\/v2\/comments?post=16773"}],"version-history":[{"count":0,"href":"https:\/\/genomequebec.com\/en\/wp-json\/wp\/v2\/posts\/16773\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/genomequebec.com\/en\/wp-json\/wp\/v2\/media\/16210"}],"wp:attachment":[{"href":"https:\/\/genomequebec.com\/en\/wp-json\/wp\/v2\/media?parent=16773"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/genomequebec.com\/en\/wp-json\/wp\/v2\/categories?post=16773"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/genomequebec.com\/en\/wp-json\/wp\/v2\/tags?post=16773"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}